Biologyarticle2026-09-23

Protocol 1: Pediatric Rare Disease Clinical Trials Inventory: A Living Scoping Review Protocol

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Abstract

Scoping review protocol to develop an inventory of pediatric rare disease clinical trials, updated on an ongoing basis, to serve as a database to support research about the design, implementation, and evaluation of such trials.

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View paper (DOI)Open access versionOpenAlexZenodo (CERN European Organization for Nuclear Research)Published 2026-09-23

Authors: Emma Iverson

Institutions: University of Ottawa