Astellas Pharma (United Kingdom)

Clinical outcome assessments in Pompe disease: a pragmatic review of their validity, concept coverage, and value in clinical practice and clinical research

Abstract Background Pompe disease is a rare, autosomal recessive, neuromuscular disorder caused by a deficiency in the acid alpha-glucosidase enzyme leading to the build-up of glycogen within lysosomes, which can result in severe cardiac, pulmonary, and skeletal disorders. The ag...

Highlights from the 17th Japan Bioanalysis Forum Symposium

The 17th Japan Bioanalysis Forum Symposium was held in Himeji, Japan, in March 2026. Under the theme "Unlock Scientific Potential: Future of Bioanalytical Expert," the symposium provided a comprehensive forum to share and discuss the latest scientific, technological, and regulato...