Janine Verstraete

Validation of proxy-reported EQ-5D-Y-3L in younger children with spinal muscular atrophy: age-related differences in performance

Abstract Objectives This study aimed to examine the psychometric performance of the proxy-reported EQ-5D-Y-3L (Y-3L) for children living with spinal muscular atrophy (SMA) aged between 5 and 12 years, with a particular focus on examining whether its properties differ across three...