Cynthia X. Qian

Retinitis Pigmentosa: A Review of Its Pathogenesis and Emerging Molecular and Cellular Therapies

Retinitis pigmentosa (RP) is the most common inherited retinal dystrophy and remains largely untreatable. This review summarizes RP pathogenesis and critically appraises emerging therapeutic strategies, including gene augmentation, gene editing, RNA-based therapies, gene-agnostic...